Non-profit discovering, developing, and providing personalized experimental ASO medicines to treat nano-rare patients — for free, for life
Carlsbad, CA
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A lot can happen in a year, and at n-Lorem, this past year has brought important milestones, new developments, and plenty to discuss at the upcoming 2026 Nano-rare Patient Colloquium. Listen to this special Colloquium preview episode here: piped.video/Jub_g7igEpI
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One Month Away!
Hear from our team about why you should join us for the 2026 Nano-rare Patient Colloquium. Registration is free!
Can’t attend in person? Join us virtually and be part of the experience from wherever you are.
nlorem.org/2026-nrpc-registr…
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One-of-a-kind art. One-of-a-kind stories.
Bid on original artwork created by n-Lorem patients and their families. Winning bids support n-Lorem and our work for Nano-rare patients.
Browse the gallery and bid: nlorem.org/auctions
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We're excited to welcome Synoligo Biotechnologies to our superb list of Nano-rare Patient Colloquium 2026 sponsors!
Synoligo enables many scientific discoveries through high-quality oligonucleotide synthesis and screening. Thank you, Synoligo, for your support!
#NRPC26
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In this Realities of the Nano-rare episode, Sally Jackson lets us into her family’s bubble, speaking candidly about the deeply complex and often terrifying realities of navigating KIF1A-associated neurological disorder.
piped.video/PK1nxTywSEI
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We’re nearly 45 days away from the biggest n-Lorem community event of the year!
Join us October 7–8 for the 2026 Nano-rare Patient Colloquium, two days dedicated to connection, shared learning, meaningful conversations, and celebrating the progress of our nano-rare community.
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Whether you join us in Cambridge or virtually, we hope to see you there. Register for free at nlorem.org.
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We’re under two months away! Come to the n-Lorem Nano-rare Patient Colloquium to connect with other families and individuals who share similar experiences.
Learn more about the #NRPC26: nlorem.org/nano-rare-patient…
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Don’t walk... run to check out the 2026 Nano-rare Patient Colloquium agenda! 🏃♀️💨
nlorem.org/nano-rare-patient…
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Throughout our lab, the Cytiva logo can be seen on equipment, boxes, and bottles. A visible reminder of the many ways Cytiva supports our work.
We’re proud to welcome @Cytiva back as a sponsor of the 2026 Nano-rare Patient Colloquium!
nlorem.org/nano-rare-patient…
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Silence ALS is an initiative that brings together Columbia University and n-Lorem to support the discovery, development, and treatment of individuals living with nano-rare genetic forms of ALS through ASO medicines.
Podcast: piped.video/2Sv0L4_EQsE
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🎨 Each canvas tells a unique story, brought to life by our talented patient artists and their families!
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We’re RNA lovers here at the n-Lorem Foundation! Happy RNA Day!
RNA plays an essential role in our work. Using antisense oligonucleotides, we can alter RNA to modify levels of protein expression, addressing the unique genetic mutations that cause nano-rare diseases.
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Experience the meaningful conversations, lasting connections, shared learning, and hope that define the Nano-rare Patient Colloquium.
Join us October 7–8 in the Boston area or virtually.
Registration is free at nlorem.org.
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Royalty Pharma joins us as a sponsor of the 2026 Nano-rare Patient Colloquium. We thank them for their commitment to n-Lorem and nano-rare patients!
The 2026 NRPC is coming soon! Join us Oct. 7-8 in Cambridge, MA.
nlorem.org/2026-nrpc-registr…
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n-Lorem Foundation retweeted
2 days left to register. Nobel laureate Dr. Drew Weissman headlines GEN's Spotlight on RNA Therapeutics this Wednesday.
📅 Wed, Jul 29 | 12–2:30 PM EDT
Join us. Free. Register: hubs.li/Q04qRxTL0
@zgives, @silvirouskin, @WeissmanLab, @n_lorem
#RNATherapeutics #RNADay #RNA
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n-Lorem is excited to announce a strategic partnership and global exclusive license agreement with @BioMarin to develop an ASO medicine for individuals living with ReNU syndrome, a serious and rare neurodevelopmental condition caused by variants in the RNU4-2 gene.
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Learn more about this collaboration: nlorem.org/biomarin-and-n-lo…
Patient group: @renusyndrome
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